Splice-Modulating Antisense Oligonucleotides as Therapeutics for Inherited Metabolic Diseases
Article in BioDrugs (January 2024)
The most recent citing publications are shown below. View all 63 publications that cite this research output on Dimensions.
Article in BioDrugs (January 2024)
Article in Biomedicines (October 2021)
Article in Scientific Reports (July 2021)